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DAY 1 ✦ LIVE: Tue, Dec 1-All Times are EST
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DAY 1 ✦ LIVE: Tue, Dec 1-All Times are EST
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10:30am-10:45am15
mins
INFORMA CONNECT-CBI AND CHAIRPERSON’S WELCOMING REMARKS
- Jenna Cerulli-Conference Producer,Informa Connect
- John Maslowski-Chief Executive Officer,Castle Creek Biosciences
10:45am-11:45am60
mins
PATIENT SPOTLIGHT ● CHASING MY CURE
- David Fajgenbaum, MD-Co-founder and Executive Director,Castleman Disease Collaborative Network
11:45am-12:30pm45
mins
EXPLORE THE CRITICAL ROLE PATIENT ADVOCACY PLAYS IN DRUG DEVELOPMENT
- Robert Coughlin-President and CEO,Massachusetts Biotechnology Council
12:30pm-1:45pm75
mins
Take Time Throughout the Day for Virtual Networking with Peers and Listen to On-Demand Sessions
1:45pm-2:30pm45
mins
PANEL ● IDENTIFY COMMON OBSTACLES IN COMPLIANT ENGAGEMENT OF PATIENTS, ADVOCATES AND CAREGIVERS
- Rahul Khara, PharmD-Vice President, Legal and Chief Compliance Officer,Acceleron Pharma Inc.
- Jennifer Helfer-former Director, Global Patient Advocacy Lead,bluebird bio
- 莉莉楼梯-Founder & Principal,Patient Authentic
CHOOSE BETWEEN FOUR CONCURRENT FEATURED TRACK SESSIONS (I-IV):
2:45pm-3:30pm45
mins
Examine Opportunities to Repurpose Current Drugs and Therapies for Rare Diseases
- Candace Lerman, JD-Founder,Rare Candace
- Monica Weldon-Founder/CEO,Bridge the Gap – SYNGAP Education and Research Foundation
- Courtney Waller-Co-Founder/Co-Director,Timothy Syndromes Alliance
- Sean Ekins-CEO,Collaborations Pharmaceuticals
2:45pm-3:30pm45
mins
Deploy Strategic Needs Assessments for Effective Reimbursement Planning and Launch
- Kim Coppom-Executive Director, Managed Markets,Relypsa
- Jen Beachell-Vice President, Commercial,Momenta Pharmaceuticals
- John Wiedemann-Director, Patient Support Services,Retrophin
2:45pm-3:30pm45
mins
Develop Key Partnerships and Channel Strategies for Product Launch
- Nick Calla-高级副甲氧苄吲酚ent, Industry Relations,Orsini Specialty Pharmacy
- David Frobel-高级副甲氧苄吲酚ent, Trade Relations,Orsini Specialty Pharmacy
2:45pm-3:30pm45
mins
Examine the Current State of Rare Disease Clinical Development and Future Predictions
- Mike Zhao-Vice President, Healthcare,MSQ Ventures
- Chris Garabedian-Chairman and CEO,Xontogeny
- Sara Nayeem, MD-Partner,NEA